Skip to main content

Pipeline

Translating data, science and technology into therapy

Silthera develops programs focused on rare and ultra-rare genetic diseases, with a specific emphasis on autosomal dominant mutations, where clinical need is high and design precision is a decisive factor

Silthera develops programs focused on rare and ultra-rare genetic diseases, with a specific emphasis on autosomal dominant mutations, where clinical need is high and design precision is a decisive factor

Candidates drugs development stages

Silthera-001

Disease Area: Visceral myopathy type 1
Target: Mutated gene associated with smooth muscle dysfunction

Discovery

Preclinical Research

Regulatory Preclinical

Clinical

Status: Regulatory Preclinical
Technology: siRNA


Silthera-002

Disease Area: Visceral myopathy type 2
Target: Mutated gene associated with smooth muscle dysfunction

Discovery

Preclinical Research

Regulatory Preclinical

Clinical

Status: Preclinical Research
Technology: siRNA


Silthera-003

Disease Area: Osteogenesis imperfecta
Target: Genetic bone disorders

Discovery

Preclinical Research

Regulatory Preclinical

Clinical

Status: Preclinical Research
Technology: siRNA


Silthera-004

Disease Area: Undisclosed

Discovery

Preclinical Research

Regulatory Preclinical

Clinical

Status: Discovery
Technology: siRNA

Partnering opportunities

Contact us

© Silthera is a trademark of Loto Biotech Platform s.r.l.
A spin-off from the University of L’Aquila

Privacy Preference Center